efficient recombinase-mediated cassette exchange in hpscs to study the hepatocyte lineage reveals aavs1 locus-mediated transgene inhibition

Clicks: 232
ID: 234861
2015
Article Quality & Performance Metrics
Overall Quality
Not rated
Combines reader engagement with the AI quality analysis. This article has not been analysed, so there is no overall score — reader engagement is measured and shown alongside.
AI Quality Assessment
Not analyzed
Readership in this journal
Steady

Ranked #35 of 101 articles by views in nature reviews gastroenterology & hepatology

Most read Least read

Bar heights use a square-root scale.

Mint this article as an NFT
Not yet minted

Create a permanent, verifiable on-chain record of this article on the Scimatic Network. The NFT is held in your Journament account, and you can withdraw it to your own wallet at any time.

5 SUSD one-off · no wallet required
Abstract
Tools for rapid and efficient transgenesis in “safe harbor” loci in an isogenic context remain important to exploit the possibilities of human pluripotent stem cells (hPSCs). We created hPSC master cell lines suitable for FLPe recombinase-mediated cassette exchange (RMCE) in the AAVS1 locus that allow generation of transgenic lines within 15 days with 100% efficiency and without random integrations. Using RMCE, we successfully incorporated several transgenes useful for lineage identification, cell toxicity studies, and gene overexpression to study the hepatocyte lineage. However, we observed unexpected and variable transgene expression inhibition in vitro, due to DNA methylation and other unknown mechanisms, both in undifferentiated hESC and differentiating hepatocytes. Therefore, the AAVS1 locus cannot be considered a universally safe harbor locus for reliable transgene expression in vitro, and using it for transgenesis in hPSC will require careful assessment of the function of individual transgenes.
Reference Key
ordovs2015stemefficient Use this key to autocite in the manuscript while using SciMatic Manuscript Manager or Thesis Manager
Authors ;Laura Ordovás;Ruben Boon;Mariaelena Pistoni;Yemiao Chen;Esther Wolfs;Wenting Guo;Rangarajan Sambathkumar;Sylwia Bobis-Wozowicz;Nicky Helsen;Jolien Vanhove;Pieter Berckmans;Qing Cai;Kim Vanuytsel;Kristel Eggermont;Veerle Vanslembrouck;Béla Z. Schmidt;Susanna Raitano;Ludo Van Den Bosch;Yaakov Nahmias;Toni Cathomen;Tom Struys;Catherine M. Verfaillie
Journal nature reviews gastroenterology & hepatology
Year 2015
DOI
10.1016/j.stemcr.2015.09.004
URL
Keywords

Citations

No citations found. To add a citation, contact the admin at info@scimatic.org

No comments yet. Be the first to comment on this article.